RARECast
Een podcast door RARECast - Donderdagen
548 Afleveringen
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A Heart Attack that Led to a Rare Disease Diagnosis
Gepubliceerd: 30-1-2025 -
Targeting Rare Liver Diseases with Gene Editing Therapies
Gepubliceerd: 23-1-2025 -
Using AI to De-Risk Rare Disease Drug Development
Gepubliceerd: 16-1-2025 -
Addressing a Growing Demand for Plasma-Derived Therapies
Gepubliceerd: 9-1-2025 -
Empowering Patients with Data to Drive Drug Development
Gepubliceerd: 2-1-2025 -
How Advocates Are Advancing a Treatment for an Ultra-Rare Disease
Gepubliceerd: 26-12-2024 -
Engineering B Cells to Produce Therapeutic Proteins
Gepubliceerd: 19-12-2024 -
A Pipeline Win as BridgeBio Learns to Balance Theory with Practice
Gepubliceerd: 12-12-2024 -
Considering What It Will Take for Payers to Embrace Advances in Sequencing
Gepubliceerd: 5-12-2024 -
Finding Strength
Gepubliceerd: 27-11-2024 -
A Non-Profit Works to Advance a DMD Gene Therapy
Gepubliceerd: 21-11-2024 -
Accepting What We Can’t Understand
Gepubliceerd: 14-11-2024 -
A Gene Therapy Company Born from a Father’s Efforts to Save his Daughter
Gepubliceerd: 7-11-2024 -
Lowering Barriers to Clinical Trial Participation with Do-It-Yourself Blood Sample Collection
Gepubliceerd: 31-10-2024 -
Scaling N-of-1 Therapies to Viability
Gepubliceerd: 24-10-2024 -
Building Gene Therapies that Address Gain and Loss of Function Simultaneously
Gepubliceerd: 17-10-2024 -
How One Woman Climbed from Patient to Advocate
Gepubliceerd: 10-10-2024 -
Shortening the Diagnostic Odyssey
Gepubliceerd: 3-10-2024 -
Making Exomes More Revealing
Gepubliceerd: 26-9-2024 -
How One Patient Organization Catalyzed Drug Development
Gepubliceerd: 19-9-2024
RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.
