RARECast
Een podcast door RARECast - Donderdagen
548 Afleveringen
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Overcoming a Delivery Challenge of Retinal Gene Therapies
Gepubliceerd: 19-6-2025 -
A Gene Editing First Augurs an Era of Bespoke Therapies
Gepubliceerd: 12-6-2025 -
How One Patient Organization Drives Drug Development
Gepubliceerd: 5-6-2025 -
Using CRISPR to Modulate Gene Expression
Gepubliceerd: 29-5-2025 -
Satisfying the Hunger for a Prader-Willi Therapy
Gepubliceerd: 22-5-2025 -
How an Academic Medical Center Helped Change the Landscape for a Rare Disease
Gepubliceerd: 15-5-2025 -
Improving Outcomes for People with a Set of Rare Cancers
Gepubliceerd: 8-5-2025 -
An Effort to Build a Better DMD Gene Therapy
Gepubliceerd: 2-5-2025 -
A Once-Failed Pain Therapy Shows Potential in a Neurodevelopmental Disorder
Gepubliceerd: 24-4-2025 -
Advancing a Cutting-Edge Therapy for a Rare, Childhood Cancer
Gepubliceerd: 17-4-2025 -
Learning to Take His Vitamins
Gepubliceerd: 10-4-2025 -
The First Treatment for a Rare Neurodegenerative Condition Awaits FDA Approval
Gepubliceerd: 3-4-2025 -
Engineering Skin Bacteria to Be Live Biotherapeutics
Gepubliceerd: 27-3-2025 -
Seeing the Gene and Cell Therapy Translational Divide as an Opportunity
Gepubliceerd: 20-3-2025 -
My Mother, Myself, and ALS
Gepubliceerd: 13-3-2025 -
From Immovable Object to Advocacy Force
Gepubliceerd: 6-3-2025 -
A Rapid and Scalable Approach for Screening Personalized ASOs
Gepubliceerd: 27-2-2025 -
Addressing the Disease Mechanism of a Rare Kidney Disease
Gepubliceerd: 20-2-2025 -
The Mother of a Son with SCD, Applies Direct Experience to Her Clinical Trials Work
Gepubliceerd: 13-2-2025 -
A First for Rett Syndrome with More in the Pipeline
Gepubliceerd: 6-2-2025
RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.
