RARECast

548 Afleveringen

1. Accelerating the Development of Genetic Medicines with AI

   Gepubliceerd: 7-12-2023
2. Leveraging AI to Address the Neuropsychiatric Conditions Associated with a Rare Disease

   Gepubliceerd: 30-11-2023
3. In Pursuit of a Treatment for His Son, A Lawyer Becomes a Biotech Executive

   Gepubliceerd: 22-11-2023
4. In Push for Treatment, a Patient Organization Becomes a Trial Sponsor

   Gepubliceerd: 16-11-2023
5. Delayed Diagnosis of Rare Diseases Takes Staggering Economic Toll

   Gepubliceerd: 9-11-2023
6. A Cell Therapy to Control Heart-Damaging Inflammation in Duchenne

   Gepubliceerd: 2-11-2023
7. Stimulating the Growth of Muscle Mass in People with Neuromuscular Diseases

   Gepubliceerd: 26-10-2023
8. Turning Grief into Action

   Gepubliceerd: 19-10-2023
9. A Plea to the FDA to Give an Ultra-Rare Disease Drug a Fair Hearing

   Gepubliceerd: 12-10-2023
10. How the Woolly Mammoth Beat a Path to Better Gene Therapies

    Gepubliceerd: 5-10-2023
11. A Genetic Counselor’s Journey into Patient Advocacy

    Gepubliceerd: 28-9-2023
12. A Company in the Fold of Rare Disease

    Gepubliceerd: 21-9-2023
13. Disabling Antibodies that Drive Rare, Immunological Conditions

    Gepubliceerd: 14-9-2023
14. Keeping the Sentinels of the Brain Vigilant

    Gepubliceerd: 7-9-2023
15. Considering the Unfinished Work in Cystic Fibrosis

    Gepubliceerd: 31-8-2023
16. How to Advocate for Yourself as You Battle Cancer

    Gepubliceerd: 24-8-2023
17. Targeting Neuroinflammation to Treat ALS

    Gepubliceerd: 17-8-2023
18. Leveraging Community Partnerships to Address a Rare Disease Behind a Medical Mystery in New Mexico

    Gepubliceerd: 10-8-2023
19. Accelerating Gene Editing Therapies for Rare, Neurological Conditions

    Gepubliceerd: 3-8-2023
20. Inhibiting Electrical Activity in Rare, Seizure Disorders

    Gepubliceerd: 27-7-2023