RARECast

548 Afleveringen

1. Improving the Function and Usability of Clothing for People with Disabilities

   Gepubliceerd: 20-7-2023
2. Treating Cardiopulmonary Disease with Inhaled Targeted Therapies

   Gepubliceerd: 13-7-2023
3. An Ally for the Undiagnosed Emerges

   Gepubliceerd: 29-6-2023
4. A Patient-Driven Registry Focused on Health-Related Quality of Life Data

   Gepubliceerd: 29-6-2023
5. Help for Rare Disease Patients That’s Just a Click Away

   Gepubliceerd: 22-6-2023
6. Diagnosing Autism with a Single Strand of Hair

   Gepubliceerd: 15-6-2023
7. Bringing Regenerative Medicine to a Rare Bone Condition in Children

   Gepubliceerd: 8-6-2023
8. Bringing Precision to CRISPR-Based Genome Editing

   Gepubliceerd: 1-6-2023
9. Capturing Patients’ Experience in Their Daily Lives

   Gepubliceerd: 25-5-2023
10. From One to Many

    Gepubliceerd: 18-5-2023
11. A Nasal Spray to Curb Excessive Eating in Prader-Willi

    Gepubliceerd: 11-5-2023
12. How One Foundation Is Laying the Groundwork to Advance Treatments for an Ultra-Rare Disease

    Gepubliceerd: 4-5-2023
13. Forging a New Path for Medicine

    Gepubliceerd: 27-4-2023
14. Restoring Hearing through Gene Therapies

    Gepubliceerd: 20-4-2023
15. Creating a Sustainable Reimbursement Model for Ultra-Rare Therapies

    Gepubliceerd: 13-4-2023
16. Lumos Hopes Its Oral Alternative to HGH Will Fuel Its Growth

    Gepubliceerd: 5-4-2023
17. Advancing a Gene Therapy for a Rare and Fatal CNS Disorder

    Gepubliceerd: 30-3-2023
18. Addressing the Barriers to Patient Participation in Clinical Trials

    Gepubliceerd: 23-3-2023
19. A Venture Philanthropist Makes the Case for Advocates Taking Equity

    Gepubliceerd: 16-3-2023
20. Seeking a Sustainable Business Developing on N-of-1 Therapies

    Gepubliceerd: 9-3-2023